Stem Cells Applications
Current Stem Cell Applications
- Bone Marrow Failure Disorders
Amegakaryocytosis
Aplastic Anemia (Severe)
Blackfan-Diamond Anemia
Congenital Cytopenia*
Congenital Dyserythropoietic Anemia
Dyskeratosis Congenita
Fanconi Anemia
Paroxysmal Nocturnal Hemoglobinuria (PNH)
Pure Red Cell Aplasia
- Hemoblobinopathies
Beta Thalassemia Major
Sickle Cell Disease
- Histiocytic Disorders
Familial Erythrophagocytic Lymphohistiocytosis
Hemophagocytosis
Langerhans Cell Histiocytosis (Histiocytosis X)
- Inherited Immune System Disorders
Chronic Granulomatous Disease
Congenital Neutropenia
Leukocyte Adhesion Deficiency
Severe Combined Immunodeficiencies (SCID) including:
Adenosine Deaminase Deficiency*
Bare Lymphocyte Syndrome
Chediak-Higashi Syndrome*
Kostmann Syndrome
Omenn Syndrome
Purine Nucleoside Phosphorylase Deficiency
Reticular Dysgenesis
Wiskott-Aldrich Syndrome
X-Linked Lymphoproliferative Disorder
- Inherited Metabolic Disorders
Adrenoleukodystrophy
Fucosidosis
Gaucher Disease*
Hunter Syndrome (MPS-II)
Hurler Syndrome (MPS-IH)
Krabbe Disease
Lesch-Nyhan Syndrome
Mannosidosis*
Maroteaux-Lamy Syndrome (MPS-VI)
Metachromatic Leukodystrophy
Mucolipidosis II (I-cell Disease)*
Neuronal Ceroid Lipofuscinosis (Batten Disease)*
Niemann-Pick Disease*
Sandhoff Disease*
Sanfilippo Syndrome (MPS-III)
Scheie Syndrome (MPS-IS)
Sly Syndrome
Tay Sachs*
Wolman Disease
- Leukemias and Lymphomas
Acute Biphenotypic Leukemia*
Acute Lymphocytic Leukemia (ALL)
Acute Myelogenous Leukemia (AML)
Acute Undifferentiated Leukemia*
Adult T Cell Leukemia/Lymphoma
Chronic Lymphocytic Leukemia (CLL)
Chronic Myelogenous Leukemia (CML)
Hodgkins Lymphoma
Juvenile Chronic Myelogenous Leukemia (JCML)
Juvenile Myelomonocytic Leukemia (JMML)
Myeloid/Natural Killer (NK) Cell Precursor Acute Leukemia
Non-Hodgkins Lymphoma
Polymphocytic Leukemia
- Myelodysplastic/Myeloproliferative Disorders
Acute Myelofibrosis*
Agnogenic Myeloid Metaplasia (Myelofibrosis)*
Amyloidosis
Chronic Myelomonocytic Leukemia (CMML)
Essential Thrombocythemia*
Polycythemia Vera*
Refractory Anemias (RA) including:
Refractory Anemia with Excess Blasts (RAEB)
Refractory Anemia with Excess Blasts in Transformation (RAEB-T)
Refractory Anemia with Ringed Sideroblasts (RARS)
- Plasma Cell Disorders
Multiple Myeloma
Plasma Cell Leukemia
Waldenstroms Macroglobulinemia
Other Inherited Disorders
Cartilage-Hair Hypoplasia
Congenital Erythropoietic Porphyria (Gunther Disease)
DiGeorge Syndrome
Osteopetrosis
- Other Malignancies
Brain Tumors**
Ewing Sarcoma*
Neuroblastoma
Ovarian Cancer*
Renal Cell Carcinoma*
Rhabdomyosarcoma
Small Cell Lung Cancer*
Testicular Cancer*
Thymoma (Thymic Carcinoma)
- Other
Chronic Active Epstein Barr
Evans Syndrome
Multiple Sclerosis*
Rheumatoid Arthritis*
Systemic Lupus Erythematosus*
Thymic Dysplasia
* in clinical trials, www. clinicaltrials.gov
Emerging Stem Cell Applications
Diabetes
Heart Disease
Liver Disease
Muscular Dystrophy
Parkinsons Disease
Spinal cord injury
Stroke